药物制剂大类 - 其他 Solid dispersion used to treat condition modulated by complement factor D e.g. paroxysmal nocturnal hemoglobinuria (PNH) and PNH with clinically evident extravascular hemolysis, comprises substantially amorphous danicopan, and polymer ❌ 缺失 用于治疗由补体因子D介导的疾病(如阵发性睡眠性血红蛋白尿症(PNH)及伴有临床明显血管外溶血的PNH)的固体分散体,包含基本无定形的danicopan和聚合物 类型 原创研究 (Original Research)